Quick Facts Field Details Active Ingredient Inebilizumab Drug Category Rare / Orphan Diseases Primary Use Neuromyelitis optica spectrum disorder — NMOSD (anti-CD19) Availability Available in Turkey ✓ Introduction Inebilizumab is...
Quick Facts Field Details Active Ingredient Avacopan Drug Category Rare / Orphan Diseases Primary Use ANCA-associated vasculitis (oral C5a receptor inhibitor) Availability Available in Turkey ✓ Introduction Avacopan is a...
Quick Facts Field Details Active Ingredient Pegcetacoplan Drug Category Rare / Orphan Diseases Primary Use Paroxysmal nocturnal hemoglobinuria (C3 inhibitor) Availability Available in Turkey ✓ Introduction Pegcetacoplan is a Rare...
Quick Facts Field Details Active Ingredient Iptacopan Drug Category Rare / Orphan Diseases Primary Use PNH (oral factor B complement inhibitor) Availability Available in Turkey ✓ Introduction Iptacopan is a...
Quick Facts Field Details Active Ingredient Eculizumab Drug Category Rare / Orphan Diseases Primary Use PNH, atypical HUS, gMG, NMOSD (C5 complement inhibitor) Availability Available in Turkey ✓ Introduction Eculizumab...
Quick Facts Field Details Active Ingredient Selepressin Drug Category Rare / Orphan Diseases Primary Use Vasopressin analogue in development Availability Available in Turkey ✓ Introduction Selepressin is a Rare /...
Quick Facts Field Details Active Ingredient Ravulizumab Drug Category Rare / Orphan Diseases Primary Use PNH, atypical HUS (long-acting C5 complement inhibitor) Availability Available in Turkey ✓ Introduction Ravulizumab is...
Quick Facts Field Details Active Ingredient Inclisiran (rare) Drug Category Rare / Orphan Diseases Primary Use Homozygous familial hypercholesterolemia (PCSK9 siRNA) Availability Available in Turkey ✓ Introduction Inclisiran (rare) is...
Quick Facts Field Details Active Ingredient Givosiran Drug Category Rare / Orphan Diseases Primary Use Acute hepatic porphyria (siRNA, targets ALAS1) Availability Available in Turkey ✓ Introduction Givosiran is a...
Quick Facts Field Details Active Ingredient Lumasiran Drug Category Rare / Orphan Diseases Primary Use Primary hyperoxaluria type 1 (siRNA) Availability Available in Turkey ✓ Introduction Lumasiran is a Rare...